
{"id":256231,"date":"2023-07-03T11:17:38","date_gmt":"2023-07-03T09:17:38","guid":{"rendered":"https:\/\/www.fqeuskadi.org\/?p=256231"},"modified":"2023-07-03T11:17:43","modified_gmt":"2023-07-03T09:17:43","slug":"trikaftaren-onurak-35-urtetik-gora-mantentzen-dira-zabalpen-saiakera-batean","status":"publish","type":"post","link":"https:\/\/www.fqeuskadi.org\/eu\/trikaftaren-onurak-35-urtetik-gora-mantentzen-dira-zabalpen-saiakera-batean\/","title":{"rendered":"Trikaftaren onurak 3,5 urtetik gora mantentzen dira zabalpen-saiakera batean"},"content":{"rendered":"<p>[et_pb_section fb_built=&#8221;1&#8243; admin_label=&#8221;section&#8221; _builder_version=&#8221;4.16&#8243; global_colors_info=&#8221;{}&#8221;][et_pb_row admin_label=&#8221;row&#8221; _builder_version=&#8221;4.16&#8243; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; global_colors_info=&#8221;{}&#8221;][et_pb_column type=&#8221;4_4&#8243; _builder_version=&#8221;4.16&#8243; custom_padding=&#8221;|||&#8221; global_colors_info=&#8221;{}&#8221; custom_padding__hover=&#8221;|||&#8221;][et_pb_text _builder_version=&#8221;4.20.4&#8243; _module_preset=&#8221;default&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<h3 class=\"p1\">Tratamenduak biriken funtzioa hobetu zuen eta biriken exazerbazio-arriskua murriztu zuen.<\/h3>\n<p class=\"p3\">Trikaftaren bidezko epe luzeko tratamenduak <b>biriken funtzioa etengabe hobetzen <\/b>du, arnas sintomak arintzen ditu eta nutrizio-egoera eragiten du Fibrosi Kistikoa (FQ)<span class=\"Apple-converted-space\">\u00a0 <\/span>eta F508del mutazioaren kopia bat duten pazienteetan.<\/p>\n<p class=\"p3\">Hala ondorioztatzen da, tratamendua sustatu duen Vertex Pharmaceuticals enpresak, Vienan (Austria) hil honetan egindako Fibrosi Kistikoaren Europako Elkartearen (ECFS) Fibrosi Kistikoari buruzko 46. Europako Konferentzian aurkeztutako datu berrietatik.<\/p>\n<p class=\"p3\">Trikaftaren hasierako onespena<b> 3. faseko bi saiakuntza klinikoren datuetan oinarritu <\/b>zen -AURORA F\/F (NCT03525548) eta AURORA F\/MF (NCT03525444)-, 12 urte edo gehiagoko plazeboa hartu zuten pazienteekin alderatu izan zirenak.<\/p>\n<p class=\"p3\">Ikerketa horien zati kontrolatua plazeboarekin amaitu ondoren, parte-hartzaileek zabalpen irekiko azterlan batean (NCT03525574) sartu ahal izan ziren. Azterketa horretan, guztiek trikafta hartu eta <b>192 astez <\/b>kontrolatu zuten (3,5 urte baino gehixeago).<\/p>\n<p class=\"p3\">Zabalpenaren emaitza osoak ECFS konferentzian aurkeztu ziren, <b>&#8220;Elexacaftor\/Tezacaftor\/Ivacaftoren (ELX\/TEZ\/IVA) epe luzeko segurtasuna eta eraginkortasuna Fibrosi Kistikoa (FQ) duten<span class=\"Apple-converted-space\">\u00a0 <\/span>eta F508alelo bat gutxienez duten pertsonengan:<span class=\"Apple-converted-space\">\u00a0 <\/span>192 asteko zabalpen irekiko azterlana\u201d<\/b><\/p>\n<p class=\"p3\"><b>Birika-funtzioa<\/b> segundo batean aurreikusitako <b>arnas bolumen bortxatuaren ehunekoa <\/b>(ppFEV1) erabiliz neurtu zen, pertsona batek arnasketa bortxatu batean kanporatu dezakeen aire-kantitatearen neurri komuna. Gaixoak trikafta hartzen hasi eta gutxira, ppFEV1en balioak igo egin ziren, batez beste 10 puntu baino gehiago.<\/p>\n<h3 class=\"p5\">Trikaftaren onurak FKa duten pazienteentzat<\/h3>\n<p class=\"p3\">Zabalpenaren emaitzek erakutsi zuten igoera hori 192 astetan mantendu zela. Hiru urte baino gehiagoko Trikafta tratamentuarekin, ppFEV1eko urteko batez besteko kanbio-tasa 0,05 baino txikiagoa izan zen. Bestela esanda, batez besteko puntuazioak ia ez ziren aldatu biriketako funtzioaren hasierako igoeraren ondoren.<\/p>\n<p class=\"p3\"><b>Arnas sintomen larritasuna <\/b>ere nabarmen hobetu zen Trikafta hasi eta gutxira, eta hiru urtez baino gehiagoz egon ziren egonkor.<b> Izerdiaren kloruro-maila<\/b> jaitsi egin zen Trikafta hasi eta gero, eta horrela iraun zuten ikerketa osoan.<\/p>\n<p class=\"p3\">\u201cIkertzaileek esan dutenez, Trikafta-ren oinarrizko saiakuntzetan behatutako<b> birika-funtzioaren<\/b>, <b>arnas sintomen<\/b> eta CFTR funtzioaren hobekuntza klinikoki esanguratsuak 192 asteko luzatze-azterketa horretan mantendu ziren\u201d.<\/p>\n<p class=\"p3\"><b>Gorputz-masaren indizea<\/b> (GMI) nabarmen handitu zen tratamenduaren lehen sei hilabeteetan. Gainerako zabalpen ikerketan, batez besteko GMI pixkanaka handituz joan zen, eta bi edo hiru urteren ondoren egoera egonkortu zen.<\/p>\n<p class=\"p3\"><a href=\"https:\/\/cysticfibrosisnewstoday.com\/news\/benefits-trikafta-cf-sustained-3-5-years-extension-trial\/\">Jatorrizko artikulua<\/a><\/p>\n<p><a href=\"https:\/\/www.fqeuskadi.org\/eu\/fdak-kalydeco-onartu-du-hilabete-batetik-aurrerako-haurrentzako\/\">Aurreko albistea: FDAk Kalydeco onartu du hilabete batetik aurrerako haurrentzako<\/a><br \/>\n[\/et_pb_text][\/et_pb_column][\/et_pb_row][\/et_pb_section]<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Tratamenduak biriken funtzioa hobetu zuen eta biriken exazerbazio-arriskua murriztu zuen. Trikaftaren bidezko epe luzeko tratamenduak biriken funtzioa etengabe hobetzen du, arnas sintomak arintzen ditu eta nutrizio-egoera eragiten du Fibrosi Kistikoa (FQ)\u00a0 eta F508del mutazioaren kopia bat duten pazienteetan. Hala ondorioztatzen da, tratamendua sustatu duen Vertex Pharmaceuticals enpresak, Vienan (Austria) hil honetan egindako Fibrosi Kistikoaren Europako [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":256227,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":""},"categories":[47],"tags":[],"class_list":["post-256231","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-fq-berriak"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v24.9 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>Trikaftaren onurak 3,5 urtetik gora mantentzen dira - FQ EUSKADI<\/title>\n<meta name=\"description\" content=\"Trikaftaren bidezko epe luzeko tratamenduak biriken funtzioa hobetzen du, arnas sintomak arintzen ditu eta nutrizio-egoeran eragiten du.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.fqeuskadi.org\/eu\/trikaftaren-onurak-35-urtetik-gora-mantentzen-dira-zabalpen-saiakera-batean\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Trikaftaren onurak 3,5 urtetik gora mantentzen dira - 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