
{"id":256162,"date":"2023-05-16T12:43:56","date_gmt":"2023-05-16T10:43:56","guid":{"rendered":"https:\/\/www.fqeuskadi.org\/?p=256162"},"modified":"2023-05-16T12:44:01","modified_gmt":"2023-05-16T10:44:01","slug":"fdak-kalydeco-onartu-du-hilabete-batetik-aurrerako-haurrentzako","status":"publish","type":"post","link":"https:\/\/www.fqeuskadi.org\/eu\/fdak-kalydeco-onartu-du-hilabete-batetik-aurrerako-haurrentzako\/","title":{"rendered":"FDAk Kalydeco onartu du hilabete batetik aurrerako haurrentzako"},"content":{"rendered":"<p>[et_pb_section fb_built=&#8221;1&#8243; admin_label=&#8221;section&#8221; _builder_version=&#8221;4.16&#8243; global_colors_info=&#8221;{}&#8221;][et_pb_row admin_label=&#8221;row&#8221; _builder_version=&#8221;4.16&#8243; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; global_colors_info=&#8221;{}&#8221;][et_pb_column type=&#8221;4_4&#8243; _builder_version=&#8221;4.16&#8243; custom_padding=&#8221;|||&#8221; global_colors_info=&#8221;{}&#8221; custom_padding__hover=&#8221;|||&#8221;][et_pb_text _builder_version=&#8221;4.20.4&#8243; _module_preset=&#8221;default&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<h3 class=\"p1\">AEBko Drogen eta Elikagaien Administrazioak, Kalydeco \u00ae onartu zuen (ivacaftor) hilabete bat eta, Kalydecora sentikortasuna frogatu duten 97 mutazioko kopia bat duten haurrentzat.<\/h3>\n<p class=\"p3\">AEBetako Drogen eta Elikagaien Administrazioa. (FDA)-k <b>Kalydeco \u00ae (ivacaftor) onartu zuen, 1-4 hilabeteko<\/b> Fibrosi Kistikoa duten eta mutazio batzuk dituzten haurrentzako. Onespen horrek haur gutxi batzuei eragiten badie ere, beste <b>urrats garrantzitsu bat<\/b> da FKa duten pertsona guztiek beren gaixotasunaren kausarako tratamendua jasoko dutela bermatzeko.<\/p>\n<blockquote>\n<p class=\"p3\">Kalydeco eta antzeko moduladoreek<b> partzialki berrezartzen dute<\/b> Fibrosi Kistikoaren (CFTR) mintzezko konduktantzia erregulatzen duen proteinaren jarduera, zeinak gatzaren eta likidoen <b>oreka egokia mantentzen baitu<\/b> biriketako eta beste organo batzuetako gainazaletan. Ikerketek erakutsi dutenez, <b>pankrearen funtzioa berrezarri<\/b> egin daiteke Kalydeco hartzen duten haur txiki batzuetan.<\/p>\n<\/blockquote>\n<h3 class=\"p3\">KALYDECO<\/h3>\n<p class=\"p3\">Kalydeco onartu zen, hasiera batean, 2012an, 6 urtetik gorako pertsonen tratamendurako G551D mutazioarekin, AEBetan FKa duten ia <b>40 000 pertsonen % 4.<\/b> Harrezkeroztik, onespena 97 mutazioetako batekinbat duten lau hilabeteko haurretara zabaldu da.<\/p>\n<p class=\"p3\">Kalydeco <b>Vertex Pharmaceuticals Inc.<\/b> enpresak garatu zuen, Cystic Fibrosis Foundation-en laguntza kliniko, zientifiko eta finantzario garrantzitsuarekin.<\/p>\n<p class=\"p3\">FKa duten pertsonei bizitza luzeagoa eta osasungarriagoa izaten laguntzeko <b>aurrerapen handia <\/b>egin den arren, pertsona batzuk ez dira hautagarriak modulatzaile bat hartzeko edo ez dute sendagaia onartzen. <b>Oraindik lan kritiko bat<\/b> egin behar da FKarekin bizi diren pertsona guztiei beren gaixotasunaren kausarako tratamendu bat lortzen laguntzeko.<\/p>\n<p><a href=\"https:\/\/www.cff.org\/news\/2023-05\/fda-approves-kalydeco-infants?utm_source=together&amp;utm_medium=email&amp;utm_campaign=kalydeco_app\">Jatorrizko albistea<\/a><\/p>\n<p>[\/et_pb_text][\/et_pb_column][\/et_pb_row][\/et_pb_section]<\/p>\n","protected":false},"excerpt":{"rendered":"<p>AEBko Drogen eta Elikagaien Administrazioak, Kalydeco \u00ae onartu zuen (ivacaftor) hilabete bat eta, Kalydecora sentikortasuna frogatu duten 97 mutazioko kopia bat duten haurrentzat. AEBetako Drogen eta Elikagaien Administrazioa. (FDA)-k Kalydeco \u00ae (ivacaftor) onartu zuen, 1-4 hilabeteko Fibrosi Kistikoa duten eta mutazio batzuk dituzten haurrentzako. Onespen horrek haur gutxi batzuei eragiten badie ere, beste urrats garrantzitsu [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":256153,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":""},"categories":[47],"tags":[],"class_list":["post-256162","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-fq-berriak"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v24.9 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>FDAk Kalydeco onartu du hilabete batetik aurrerako haurrentzako<\/title>\n<meta name=\"description\" content=\"AEBko Drogen eta Elikagaien Administrazioak, Kalydeco \u00ae onartu zuen hilabete bat eta, Kalydecora sentikortasuna duten 97 mutazioentzat.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.fqeuskadi.org\/eu\/fdak-kalydeco-onartu-du-hilabete-batetik-aurrerako-haurrentzako\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"FDAk Kalydeco onartu du hilabete batetik aurrerako haurrentzako\" \/>\n<meta property=\"og:description\" content=\"AEBko Drogen eta Elikagaien Administrazioak, Kalydeco \u00ae onartu zuen hilabete bat eta, Kalydecora sentikortasuna duten 97 mutazioentzat.\" \/>\n<meta property=\"og:url\" content=\"https:\/\/www.fqeuskadi.org\/eu\/fdak-kalydeco-onartu-du-hilabete-batetik-aurrerako-haurrentzako\/\" \/>\n<meta property=\"og:site_name\" content=\"FQ EUSKADI - 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